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This newsletter contains 100% positive biotech vibes. You may wonder, what has happened to Adam?
A moment to recognize some hopeful news
The 75% slowing of disease progression reported by Uniqure with its Huntington’s disease gene therapy AMT-130 was the kind of stop-reading-and-gasp moment that crystalizes the profound impact these types of one-time treatments can have for patients dealing with rare diseases.
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